Abeona Therapeutics provides clinical update on MPS IIIA gene therapy trial
Abeona announced updated clinical data from the Phase 1/2 trial for ABO-102 (AAV-SGSH), the company’s clinical gene therapy for treatment of Sanfilippo syndrome type A. The ongoing ABO-102 trial results demonstrate robust and durable clinical effects achieved throughout various timepoints. May 18, 2018